What Is the Most Expensive Prescription Drug and Why Does It Cost $2.1 Million?

Discover why Zolgensma is the most expensive prescription drug, costing $2.1 million, and how it treats spinal muscular atrophy in children.

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The most expensive prescription drug is Zolgensma, used to treat spinal muscular atrophy (SMA). With a one-time treatment cost of approximately $2.1 million, it is engineered to provide a functional copy of the human SMN gene, ultimately offering life-changing benefits for children under two years old with SMA. Its high price is attributed to the transformative impact it can have on patients' lives.

FAQs & Answers

  1. What is Zolgensma used to treat? Zolgensma is used to treat spinal muscular atrophy (SMA), a genetic disorder that affects muscle strength and movement in young children.
  2. Why does Zolgensma cost over $2 million? Zolgensma's high cost is due to its groundbreaking gene therapy technology and its life-changing benefits as a one-time treatment for a rare and severe disease.
  3. How does Zolgensma work to treat SMA? Zolgensma provides a functional copy of the human SMN gene to patients, helping to restore muscle function and slow disease progression in children under two years old.

Watch More

For further insights, explore related content on groundbreaking gene therapies, the economics behind expensive drugs, and advances in treating rare genetic disorders like spinal muscular atrophy.

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